Translarna

Indicated For

Nonsense mutation Duchenne muscular dystrophy (nmDMD)

About This Medication

# PTC Therapeutics Patient Assistance Program Guide: Getting Translarna at Low Cost ## Overview Translarna (ataluren) is a specialized medication for nonsense mutation Duchenne muscular dystrophy (nmDMD). Because this is a rare condition requiring an expensive treatment, PTC Therapeutics offers a Patient Assistance Program (PAP) to help eligible patients access Translarna at reduced or no cost. ## Who Can Apply? You may qualify for the PTC Therapeutics Patient Assistance Program if you: - Have a valid prescription for Translarna from your doctor - Are a U.S. resident - Meet the program's income requirements - Have insurance gaps or cannot afford your medication costs ## Income Eligibility Income limits vary based on your household size and circumstances. The program uses federal poverty guidelines as a baseline but adjusts limits based on individual situations. Your income threshold may be higher if you have: - Multiple dependents - Significant out-of-pocket medical expenses - Other financial hardships During your application, you'll provide proof of income, and the program will determine your specific eligibility. There is no single income cutoff—eligibility is assessed individually. ## Insurance Coverage The PAP works with most insurance types, including: - Private insurance plans - Medicare (for eligible beneficiaries) - Medicaid - Military coverage (TRICARE) - Uninsured patients If you have insurance, the program may help cover your copayments, coinsurance, or deductibles. If you're uninsured, the program may provide Translarna at no cost or a greatly reduced price. ## Savings Card Option The program also offers a savings card that may reduce your out-of-pocket costs at the pharmacy. This option can be faster than the full assistance program and doesn't require income verification. Ask your pharmacist if you qualify for the savings card before applying for full patient assistance. ## What You'll Need to Apply Gather these documents before applying: **1. Valid Prescription** - A current prescription from your neurologist or treating physician - The prescription should specify Translarna and your dosage **2. Proof of Income** - Recent pay stubs (last 2 months) - Tax returns from the previous year - Social Security statements - Unemployment benefits documentation - If self-employed: business tax returns or profit/loss statements **3. Proof of Residency** (optional but helpful) - Utility bill or lease agreement ## 4-Step Application Process **Step 1: Contact the Program** Reach out to PTC Therapeutics Patient Assistance Program through your doctor's office or pharmacy. Many prescribers have experience with this program and can help initiate the application. **Step 2: Submit Your Application** Complete the application form with your personal, financial, and prescription information. Include all supporting documents listed above. Your healthcare provider may submit this on your behalf. **Step 3: Verification** The program reviews your application, verifies income, and confirms insurance status. This typically takes 5-10 business days. **Step 4: Approval and Access** Once approved, you'll receive authorization. Your pharmacy will be notified, and you can pick up your medication with reduced or no copayment. ## Timeline Expectations - **Application submission to approval:** 5-10 business days (standard) - **Expedited review:** 1-2 business days (if medically necessary) - **Re-authorization:** Not required—once approved, you remain enrolled as long as your circumstances don't change ## Important Notes **No Re-authorization Required** Unlike some assistance programs, you won't need to reapply annually if your situation remains stable. Notify the program only if your income or insurance changes significantly. **Prescription Refills** Your prescription must remain current with your doctor. Work with your healthcare provider to ensure timely refill authorizations so your medication doesn't lapse. ## What If You're Denied? If your application is denied, ask why. Common reasons include: - Income exceeds program limits - Missing documentation - Insurance covers the full cost You can reapply if your circumstances change, or ask about the savings card as an alternative. ## Get Started Today Don't delay treatment due to cost concerns. Contact your doctor or pharmacist to begin the application process. The PTC Therapeutics Patient Assistance Program is designed to ensure that nmDMD patients can access Translarna regardless of financial barriers.

Program information last verified: March 25, 2026