EMFLAZA

Indicated For

Duchenne Muscular Dystrophy (DMD)

About This Medication

# PTC Cares Patient Assistance Program: How to Get EMFLAZA at Low or No Cost ## About EMFLAZA (Deflazacort) EMFLAZA (deflazacort) is a prescription medication used to treat certain rare diseases. PTC Therapeutics, the manufacturer, recognizes that medication costs can be a significant barrier to treatment. The **PTC Cares Patient Assistance Program** is designed to help eligible patients access EMFLAZA at low or no cost, ensuring that financial constraints don't prevent you from receiving the care you need.[1][3] ## Who Qualifies for PTC Cares? The PTC Cares program is specifically designed for **uninsured or underinsured patients** who meet income guidelines.[3] You may be eligible if: - You are uninsured (have no health insurance coverage) - You are underinsured (have insurance but face high out-of-pocket costs) - Your household income falls within the program's income thresholds - You have a valid prescription for EMFLAZA from a licensed U.S. healthcare provider - You are a resident of the United States or Puerto Rico[3] ### Income Eligibility While specific income thresholds are not publicly listed, the program typically serves families with household incomes up to **400-500% of the federal poverty level**.[3] This means the program accommodates a wide range of income levels. For example, a family of four earning up to approximately $115,000-$145,000 annually may qualify, though exact limits depend on current federal poverty guidelines. To determine your specific eligibility, a dedicated Case Manager will review your financial situation during the enrollment process.[1] ## Insurance Requirements The program is designed for patients who are: - **Completely uninsured** (no health insurance at all) - **Underinsured** (have insurance but with high deductibles, copays, or coverage denials) If you have commercial insurance, Medicare, or Medicaid, you may still qualify if your out-of-pocket costs are substantial or if your insurance denies coverage.[1][3] The program works alongside your existing insurance to minimize your costs. ## How to Apply: Step-by-Step ### Step 1: Get a Prescription Work with your healthcare provider to obtain a valid prescription for EMFLAZA. Your provider must be a licensed U.S. healthcare professional.[1] ### Step 2: Complete the Prescription Start Form You and your healthcare provider will complete the **EMFLAZA Prescription Start Form** together. This form collects essential information about you, your prescription, and your authorization for PTC to process your enrollment.[2] ### Step 3: Gather Required Documents Before submitting, prepare the following: - Completed Prescription Start Form (signed by you and your provider) - Copies of both sides of your insurance card (if you have insurance) - Copies of both sides of your prescription benefit card (if applicable) - HIPAA authorization signature - Proof of household income (for income verification)—such as recent pay stubs, tax returns, or Social Security award letters[9] ### Step 4: Submit Your Application Fax your completed form and supporting documents to: **Fax: 1-844-322-9980** Include all required documents to prevent processing delays.[2] ### Step 5: Case Manager Contact Once received, a dedicated Case Manager from PTC Cares will contact you to: - Verify your insurance coverage and benefits - Review your income eligibility - Explain any additional financial assistance programs you may qualify for - Answer your questions about the enrollment process[1] ### Step 6: Receive Your Medication Once approved, your medication will be shipped to you through a specialty pharmacy designated by PTC Cares. Your Case Manager will coordinate all delivery details.[1] ## Bridge Program: Immediate Access If you are currently receiving EMFLAZA through importation from outside the United States, you may qualify for the **Bridge Program**. This program provides EMFLAZA free of charge while your insurance status is being investigated, ensuring no interruption in your therapy.[6] ## Timeline and Delivery PTC Cares is committed to getting you medication as quickly as possible. While specific processing timelines are not publicly stated, the program prioritizes rapid enrollment and delivery. Your Case Manager will keep you informed throughout the process. Once approved, medication is **shipped directly to you** through a specialty pharmacy partner.[1] ## What Happens If Your Application Is Denied If you are initially denied, your Case Manager will: - Explain the reason for denial - Discuss alternative financial assistance programs that may be available - Help you understand next steps You may also contact PTC Cares directly to discuss your situation and explore other options.[1] ## Reauthorization and Ongoing Support Your enrollment in PTC Cares is not a one-time process. The program provides **ongoing support** through your Case Manager, who will: - Monitor your insurance coverage - Help with prescription refills - Reassess your eligibility as needed - Connect you with additional resources, including the Peer Navigator Program to speak with other families on similar journeys[1] ## Getting Help For questions or to get started, contact PTC Cares: **Phone: 1-844-4PTCCARES (1-844-478-2227)** **Hours: Monday-Friday, 8 AM - 6 PM ET** **Website: PTCCares.com** You can also request to speak with an **English- or Spanish-speaking navigator** based on your preference.[1] ## Important Disclaimer This guide provides general information about the PTC Cares Patient Assistance Program. Program eligibility, benefits, and requirements may change. For the most current and accurate information, contact PTC Cares directly or visit PTCCares.com. This information is not a guarantee of program enrollment or medication access. Always consult with your healthcare provider about your treatment options.

Program information last verified: March 30, 2026